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- New Patient Resource Hub:<\/b> Arrowhead expands its We\u2019ll Get There Soon<\/i> campaign with the launch of a dedicated patient website, providing education, tools, and support for those living with FCS and extremely high triglycerides\n<\/li>\n
- Amplifying Patient Voices:<\/b> The Spotlight on FCS<\/i> white paper shares real patient experiences, highlighting the challenges of managing this ultra-rare disease and the need for greater awareness\n<\/li>\n
- Commitment to the FCS Community:<\/b> On Rare Disease Day and beyond, Arrowhead remains dedicated to elevating patient voices and fostering community engagement. #ForFCS\n<\/li>\n<\/ul>\n
PASADENA, Calif.–(BUSINESS WIRE<\/a>)–
\nArrowhead Pharmaceuticals, Inc. (NASDAQ: ARWR) marks Rare Disease Day with the expansion of the We\u2019ll Get There Soon<\/i> campaign, initially launched for healthcare providers in November 2024. This new phase introduces a dedicated educational website, www.LowerMyTGs.com<\/a>, and the Spotlight on FCS<\/i> white paper, which provides essential resources and support for those affected by Familial Chylomicronemia Syndrome (FCS).<\/p>\nThis press release features multimedia. View the full release here: https:\/\/www.businesswire.com\/news\/home\/20250228568692\/en\/<\/a><\/p>\n
![\"The](\"https:\/\/mms.businesswire.com\/media\/20250228568692\/en\/2396077\/4\/The_Power_of_Knowing.jpg\")
<\/p>\nThe Power of Knowing: Living with Familial Chylomicronemia Syndrome (FCS) http:\/\/www.lowermytgs.com\/ (Graphic: Business Wire)<\/p>\n<\/div>\n
\nFCS is an ultra-rare genetic disorder that significantly impairs the body’s ability to process triglycerides, leading to dangerously high triglyceride (TG) levels \u2014 typically exceeding 880 mg\/dL \u2014 and increasing the risk of life-threatening complications, such as acute pancreatitis. Because of this risk, expert guidelines recommend maintaining triglyceride levels below 500 mg\/dL. FCS remains widely underdiagnosed and is estimated to affect between 1 and 13 people per million globally. To address this gap, Arrowhead\u2019s new initiatives aim to amplify patient voices, foster community, and provide accessible educational tools.<\/p>\n
\nArrowhead\u2019s new patient website serves as a comprehensive resource for those affected by FCS and extremely high triglycerides. It provides educational content, patient testimonials, and opportunities for community connection. Additionally, the Spotlight on FCS<\/i> white paper, developed with engagement and support of the FCS Foundation, Action FCS, and FH Europe Foundation, captures firsthand patient experiences, highlighting key challenges in disease management and aiming to drive greater awareness and action.<\/p>\n
\nOne such patient testimonial can be found on the patient website here<\/a>.<\/p>\n
\n\u201cIn recognition of Rare Disease Day, we prioritize giving the FCS community a voice. Arrowhead\u2019s Spotlight on FCS<\/i> white paper, which highlights what life looks like for those living with this ultra-rare condition, is a novel look at how these individuals are navigating life with FCS,\u201d said Lindsey Sutton, co-founder of the FCS Foundation. \u201cThis paper is a major contribution to the community as it sheds a light on the unmet needs patients face with their disease from their firsthand experiences.\u201d<\/p>\n
\nAndy Davis, Senior Vice President, Global Cardiometabolic Franchise at Arrowhead, added, \u201cFor nearly two decades, Arrowhead has been dedicated to advancing RNAi-based therapies to address challenging diseases. These new resources reaffirm our commitment to the FCS community by enhancing awareness, support, and access to information through the expansion of the We\u2019ll Get There Soon<\/i> campaign.\u201d<\/p>\n
\nExplore the new resources at www.LowerMyTGs.com<\/a>.<\/p>\n
\n#ForFCS #RareDiseaseDay #WellGetThereSoon<\/p>\n
About Familial Chylomicronemia Syndrome<\/b><\/p>\n
\nFamilial chylomicronemia syndrome (FCS) is a severe and rare disease often caused by various monogenic mutations. FCS leads to extremely high triglyceride (TG) levels, typically over 880 mg\/dL. Such severe elevations can lead to various serious signs and symptoms including acute and potentially fatal pancreatitis, chronic abdominal pain, diabetes, hepatic steatosis, and cognitive issues. Currently, there are limited therapeutic options to adequately treat FCS.<\/p>\n
About the FCS Foundation<\/b><\/p>\n
\nEstablished in 2016 by two disease advocates directly impacted by FCS, the FCS Foundation connects the FCS community and provides resources and support for those with FCS. The Foundation hosts an annual Patient & Caregiver Meeting and works year-round to raise awareness and advocate for FCS. The Foundation operates as an all-volunteer organization alongside a medical advisory board of specialists working to advance future treatments. In Spring 2025, the Foundation will have expanded patient resources available for the community. For more information about the Foundation’s mission and initiatives, please visit their official website at livingwithfcs.org<\/a>.<\/p>\n
About Arrowhead Pharmaceuticals<\/b><\/p>\n
\nArrowhead Pharmaceuticals develops medicines that treat intractable diseases by silencing the genes that cause them. Using a broad portfolio of RNA chemistries and efficient modes of delivery, Arrowhead therapies trigger the RNA interference mechanism to induce rapid, deep, and durable knockdown of target genes. RNA interference, or RNAi, is a mechanism present in living cells that inhibits the expression of a specific gene, thereby affecting the production of a specific protein. Arrowhead\u2019s RNAi-based therapeutics leverage this natural pathway of gene silencing.<\/p>\n
\nFor more information, please visit www.arrowheadpharma.com<\/a>, or follow us on X (formerly Twitter) at @ArrowheadPharma<\/a>, LinkedIn<\/a>, Facebook<\/a>, and Instagram<\/a>. To be added to the Company’s email list and receive news directly, please visit http:\/\/ir.arrowheadpharma.com\/email-alerts<\/a>.<\/p>\n
Safe Harbor Statement under the Private Securities Litigation Reform Act:<\/b><\/p>\n
This news release contains forward-looking statements within the meaning of the “safe harbor” provisions of the Private Securities Litigation Reform Act of 1995. Any statements contained in this release except for historical information may be deemed to be forward-looking statements. Without limiting the generality of the foregoing, words such as \u201cmay,\u201d \u201cwill,\u201d \u201cexpect,\u201d \u201cbelieve,\u201d \u201canticipate,\u201d \u201chope,\u201d \u201cintend,\u201d \u201cplan,\u201d \u201cproject,\u201d \u201ccould,\u201d \u201cestimate,\u201d \u201ccontinue,\u201d \u201ctarget,\u201d \u201cforecast\u201d or \u201ccontinue\u201d or the negative of these words or other variations thereof or comparable terminology are intended to identify such forward-looking statements. In addition, any statements that refer to projections of our future financial performance, trends in our business, expectations for our product pipeline or product candidates, including anticipated regulatory submissions and clinical program results, prospects or benefits of our collaborations with other companies, or other characterizations of future events or circumstances are forward-looking statements. These forward-looking statements include, but are not limited to, statements about the initiation, timing, progress and results of our preclinical studies and clinical trials, and our research and development programs; our expectations regarding the potential benefits of the partnership, licensing and\/or collaboration arrangements and other strategic arrangements and transactions we have entered into or may enter into in the future; our beliefs and expectations regarding milestone, royalty or other payments that could be due to or from third parties under existing agreements; and our estimates regarding future revenues, research and development expenses, capital requirements and payments to third parties. These statements are based upon our current expectations and speak only as of the date hereof. Our actual results may differ materially and adversely from those expressed in any forward-looking statements as a result of numerous factors and uncertainties, including the impact of the ongoing COVID-19 pandemic on our business, the safety and efficacy of our product candidates, decisions of regulatory authorities and the timing thereof, the duration and impact of regulatory delays in our clinical programs, our ability to finance our operations, the likelihood and timing of the receipt of future milestone and licensing fees, the future success of our scientific studies, our ability to successfully develop and commercialize drug candidates, the timing for starting and completing clinical trials, rapid technological change in our markets, the enforcement of our intellectual property rights, and the other risks and uncertainties described in our most recent Annual Report on Form 10-K, subsequent Quarterly Reports on Form 10-Q and other documents filed with the Securities and Exchange Commission from time to time. We assume no obligation to update or revise forward-looking statements to reflect new events or circumstances.<\/i><\/p>\n
Source: <\/b>Arrowhead Pharmaceuticals, Inc.<\/p>\n
<\/p>\n
View source version on businesswire.com: <\/span>https:\/\/www.businesswire.com\/news\/home\/20250228568692\/en\/<\/a><\/span><\/p>\n
\nArrowhead Pharmaceuticals, Inc.
\n
Vince Anzalone, CFA
\n
626-304-3400
\n
ir@arrowheadpharma.com<\/a><\/p>\nInvestors:
\n<\/b>
LifeSci Advisors, LLC
\n
Brian Ritchie
\n
<\/span>212-915-2578
\n
britchie@lifesciadvisors.com<\/a><\/p>\nMedia:
\n<\/b>
LifeSci Communications, LLC
\n
Kendy Guarinoni, Ph.D.
\n
724-910-9389
\n
kguarinoni@lifescicomms.com<\/a><\/p>\nKEYWORDS:<\/b> United States North America California<\/p>\n
INDUSTRY KEYWORDS:<\/b> Health Diabetes Genetics General Health Pharmaceutical Biotechnology<\/p>\n
- Amplifying Patient Voices:<\/b> The Spotlight on FCS<\/i> white paper shares real patient experiences, highlighting the challenges of managing this ultra-rare disease and the need for greater awareness\n<\/li>\n
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